Avidity Biosciences Honors Rare Disease Day®

SAN DIEGO, Feb. 28, 2023 /PRNewswire/ -- Avidity Biosciences, Inc. (Nasdaq: RNA), a biopharmaceutical company committed to delivering a new class of RNA therapeutics called Antibody Oligonucleotide Conjugates (AOCs™), today announced its support for Rare Disease Day®, highlighting the importance of bringing awareness to the devastating impact rare diseases have on patients, families and caregivers.

"This Rare Disease Day, we join with others around the world to show our commitment in bringing awareness to rare diseases. Today, we are honored to welcome members from our patient advisory council to Avidity as part of our commitment to listening, learning, and partnering with the patient community," said Sarah Boyce, president and chief executive officer at Avidity. "We look forward to our continued collaboration with the patient and advocacy communities as we advance our three rare disease programs in DM1, FSHD and DMD with the ultimate goal of profoundly improving people's lives by revolutionizing the delivery of RNA therapeutics."

Avidity has three distinct rare disease programs in clinical development: AOC 1001 for myotonic dystrophy type 1 (DM1) in the Phase 1/2 MARINA™ trial and the MARINA open label extension (MARINA-OLE™); AOC 1020 in the Phase 1/2 FORTITUDE™ trial for the treatment of facioscapulohumeral muscular dystrophy (FSHD); and AOC 1044 in the Phase 1/2 EXPLORE44™ trial for the treatment of Duchenne muscular dystrophy (DMD) mutations amenable to Exon 44 skipping (DMD44).

"Rare Disease Day is an important time of recognition for the continued commitment and ongoing work from those organizations and individuals in the rare disease fight," said Charlene Son Rigby, CEO at Global Genes. "This day has always been important for the rare community as a time of unity and one which inspired hope for all."